Rare Childhood Disorder Gets Its First FDA Drug Approval

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Source: MedPage Today

Original: https://www.medpagetoday.com/neurology/generalneurology/119404...

Published: Tue, 13 Jan 2026 15:47:18 -0500

The FDA has approved the drug copper histidinate (Zycubo) as the first treatment for Menkes disease in pediatric patients. It is a rare childhood disorder. The agency announced the approval on Monday. The treatment is a subcutaneous injection formulation of copper histidine. The goal of the drug is to deliver between the body of patients. This is the first FDA approval of a drug for this disease. The information was published by MedPage Today.